QURE Submits Application for Gene Therapy for Huntington's Disease
UniQure NV (QURE) has submitted an application seeking accelerated FDA approval for its gene therapy AMT-130 for Huntington's disease. The company is also pursuing Priority Review and a regulatory filing in the U.K., adding momentum to its regulatory efforts.
Why it matters — A QURE watcher would care because the regulatory submissions for AMT-130 represent a significant step forward in the pipeline for this gene therapy candidate.