Precision BioSciences Commences Dosing in Phase 1/2 FUNCTION-DMD Study
Precision BioSciences announced that the first patient was dosed in August in its Phase 1/2 FUNCTION-DMD clinical trial, which evaluates PBGENE-DMD for the treatment of Duchenne muscular dystrophy. PBGENE-DMD is the company's wholly owned in vivo gene editing program built on its ARCUS platform.
Why it matters — This marks an important clinical milestone for Precision's lead wholly owned in vivo gene editing program, advancing it into patient evaluation for a serious unmet-need disease.